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Spark Therapeutics Announces Collaboration with Leading Gene Therapy Center at University of Massachusetts Medical School

PHILADELPHIA, Oct. 20, 2016 (GLOBE NEWSWIRE) -- Spark Therapeutics (ONCE), a fully integrated gene therapy company seeking to transform the lives of patients with debilitating genetic diseases by developing investigational, potentially one-time, life-altering treatments, announced today a multi-year research agreement with Guangping Gao, Ph.D., the Penelope Booth Rockwell Chair in Biomedical Research, director of the Horae Gene Therapy Center, and professor of microbiology and physiological systems at the University of Massachusetts Medical School. Dr. Gao will collaborate broadly with Spark Therapeutics to identify adeno-associated virus (AAV) vectors from a proprietary library of AAV capsids and evaluate their efficacy, with the goal of enhancing the efficiency of gene delivery to cells in the retina, liver and central nervous system.

“We’re excited to have selected Spark Therapeutics as a collaborator to develop next-generation AAV vectors that deliver genetic information to certain cell types more efficiently and to cell types that are otherwise hard to target,” said Dr. Gao, an internationally renowned AAV and gene therapy researcher.

Under the agreement, Spark Therapeutics has the option to an exclusive, world-wide license for the intellectual property...


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